University of California: Gene Therapy Delivers Lasting Immune Protection in Children With Rare Disorder
October 16, 2025
October 16, 2025
LOS ANGELES, California, Oct. 16 (TNSjou) -- The University of California issued the following news release:
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Gene therapy delivers lasting immune protection in children with rare disorder
Long-term follow-up shows 95% success rate, no serious complications in largest ADA-SCID gene therapy study to date
Key takeaways
* A blood stem cell gene therapy co-developed by UCLA's Dr. Donald Kohn restored immune function in 59 of . . .
* * *
Gene therapy delivers lasting immune protection in children with rare disorder
Long-term follow-up shows 95% success rate, no serious complications in largest ADA-SCID gene therapy study to date
Key takeaways
* A blood stem cell gene therapy co-developed by UCLA's Dr. Donald Kohn restored immune function in 59 of . . .