Saturday - March 28, 2026

Public Policy Tipoffs Involving Florida

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UM Miller School of Medicine: A Promising Gene Therapy for Older Children With Duchenne Muscular Dystrophy
MIAMI, Florida, Dec. 27 (TNSres) -- The University of Miami Miller School of Medicine issued the following news: A new gene therapy, ELEVIDYS, has been approved to treat older Duchenne muscular dystrophy (DMD) patients. UHealth--University of Miami Health System and Holtz Children's Hospital physicians are playing a major role in getting them access. The therapy delivers a functional micro-gene to muscle cells, potentially arresting DMD progression and, in some cases, possibly reversing it.   more